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Useful links about rare diseases
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1
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48
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November 18, 2024
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Regulatory sandboxes: A new frontier for rare disease therapies (IRDiRC Publication )
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0
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7
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October 23, 2025
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N-of-1 therapy development
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8
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118
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August 6, 2025
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World Orphan Drug Congress 2025 | event
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0
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7
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July 15, 2025
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Webinar: “Clinical Trials in Focus: Innovations and Patient Perspectives in Rare Diseases”
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0
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15
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February 24, 2025
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Is the drug that I want to prescribe reimbursed?
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1
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37
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February 18, 2025
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Patient recorded outcome measurements (PROMs) for rare diseases
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1
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29
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February 13, 2025
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Orphan Drug designation
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2
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55
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February 6, 2025
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Patientregistries on rare disease
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4
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26
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February 4, 2025
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Difference Orphan designation and marketing authorisation
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1
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52
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February 4, 2025
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Financiering voor onderzoek naar gepast gebruik / Funding for research on optimizing medication use
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1
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30
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January 28, 2025
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Open Academy Schools | EURODIS
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0
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13
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January 27, 2025
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Rare2025 | Vienna, Austria
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0
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31
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January 24, 2025
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Nationale Conferentie Zeldzame Aandoeningen 2025 | VSOP & NFU
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0
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16
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January 17, 2025
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Zeldzameziektendag NL
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0
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13
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January 10, 2025
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FDA-NIH Rare disease day, USA - February 27-28
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0
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17
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January 7, 2025
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Non-coverage of medication for a rare disease
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0
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22
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November 1, 2024
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RE(ACT) Congress
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0
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12
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October 10, 2024
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